Visual Recovery and Neurological Stabilization Following Miglustat Treatment in Pediatric CLN3 Disease
Published online on September 18, 2025
Abstract
Journal of Child Neurology, Volume 41, Issue 5, Page 636-646, May 2026.
Neuronal ceroid lipofuscinosis type 3 (CLN3) disease is a rare, life-limiting pediatric neurodegenerative disorder with no approved disease-modifying therapy. We conducted a prospective case report from October 2023 to April 2025 involving two female ...
Neuronal ceroid lipofuscinosis type 3 (CLN3) disease is a rare, life-limiting pediatric neurodegenerative disorder with no approved disease-modifying therapy. We conducted a prospective case report from October 2023 to April 2025 involving two female ...