PRO-ADD: Patient-empowered dose-finding trials integrating safety, preliminary efficacy and patient-reported outcomes for optimal dose selection
Statistical Methods in Medical Research: An International Review Journal
Published online on April 30, 2026
Abstract
Statistical Methods in Medical Research, Ahead of Print.
Advances in oncology drug development are driving the emergence of novel therapies, challenging traditional dose-efficacy assumptions in dose-finding oncology trials. Traditional trial designs aim to identify a maximum tolerated dose (MTD) by assessing ...
Advances in oncology drug development are driving the emergence of novel therapies, challenging traditional dose-efficacy assumptions in dose-finding oncology trials. Traditional trial designs aim to identify a maximum tolerated dose (MTD) by assessing ...